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The project

From discovery to remission

A breakthrough technology, an advanced clinical program in humans, validation in animals, and a pipeline leading to Phase 2. Here is how it all fits together.

2013 – 2018

The MYASTERIX consortium

A 5-year European collaborative project that advanced the targeted active therapy (granted orphan drug designation) against myasthenia gravis: clinical safety, immunogenicity, and efficacy.

Supported by the European Commission under the 7th Framework Programme (FP7) — grant agreement No. 602420.

Subvention CE · 6 M€ Budget total · 7,5 M€ 6 partenaires
  • CuraVac Europe Belgium
  • UZA · Antwerp Belgium
  • LUMC · Leiden Netherlands
  • piCHEM Austria
  • Aepodia Belgium
  • Inserm Transfert France

Human development

The Phase 1b clinical trial

In 2016, at Antwerp University Hospital (UZA), 24 patients with mild to moderate myasthenia gravis received CV-MG01. This first-in-human proof-of-concept study aimed to measure the safety, tolerability, and immunogenic response of the candidate.

Protocol

Three cohorts of 8 patients. In each, 6 receive the immunization and 2 a placebo. Low dose in the first cohort, then high dose in the next two.

Cohort 1

Low dose

6 immunized · 2 placebo

Cohort 2

High dose

6 immunized · 2 placebo

Cohort 3

High dose

6 immunized · 2 placebo

CV-MG01 Placebo (aluminum hydroxide)

24

patients (UZA, 2016)

4

became asymptomatic

3

remained so > 4 years

Tolerability · excellent profile

Adverse events mostly mild to moderate, mainly injection-site reactions that resolved spontaneously within a few days.

Signs of efficacy

Most patients improved · 4 became asymptomatic, 3 of whom remained so for more than 4 years. The strongest antibody responders are also the most improved.

These results — an excellent tolerability profile together with signs of efficacy — call for a Phase 2 efficacy trial with a more potent formulation, CV-MG02. Efficacy remains to be confirmed in Phase 2.

Key milestones

Phase 1b

successful · safety (UZA, 2018).

EMA · FDA

orphan drug (2009, 2011).

75%

remission in dogs with complementary peptides.

€18 M

in channeled funding.

Next step: the Phase 2 efficacy trial

With CV‑MG02, a more potent formulation, we are now seeking investors to fund this decisive next step in development.